- Jackie Bower; UNC; https://www.med.unc.edu/ophth/directory/jacquelyn-j-bower-phd/
- Chengwen Li; UNC; https://www.med.unc.edu/genetherapy/research-laboratories/li-lab/
- Brian Gilger; NC State; https://gilgerlab.cvm.ncsu.edu/
- Bryan Sutton; Texas Tech; http://www.ttuhsc.edu/som/physiology/faculty/sutton/
- Jude Samulski; UNC; https://www.med.unc.edu/pharm/people/primaryfaculty/richard-j-samulski-1
- Joanne Kurtzberg; Duke; http://autismcenter.duke.edu/content/joanne-kurtzberg-md
- Isabelle Richard; Genethon; https://integrare-umrs951.jimdo.com/home/labs/progressive-muscular-dystrophy/
- Miracles in Sight; https://www.miraclesinsight.org/
- Jain Foundation; https://www.jain-foundation.org/
- National MPS1 Society; https://mpssociety.org/learn/diseases/mps-i
- Nate Hathaway; UNC; https://pharmacy.unc.edu/research/faculty-labs/nate-hathaway-lab/
- Bedrock Therapeutics; https://bedrocktherapeutics.com/
- Astro Therapeutics
- Graybug Vision; https://www.graybug.vision/
- Epigenos Biosciences